This video shows the breathtaking improvements that one child gained from Nusinersen. He never stood or walked before receiving Nusinersen. He continues to gain strength and function, recently learning to ride a bike.
- This is the heartbreaking natural progression of SMA in 1 year in a type 2 child
- Nusinersen data showing a significant departure from the natural course of disease progression with SMA Type 2 and Type 3